Presentations & Publications

Preliminary Results from a First-in-Human Phase I/II Gene Therapy Study (FOCUS) of Subretinally Delivered GT005, an Investigational AAV2 Vector, in Patients With Geographic Atrophy Secondary to Age-Related Macular Degeneration

DateJul 16, 2022

Conference/JournalAmerican Society of Retina Specialists 2022

Szilárd Kiss, MD read more

Preliminary Results from a First-in-Human Phase I/II Gene Therapy Trial (FOCUS) of Subretinally Delivered GT005, an Investigational AAV2 Vector, in Patients with Geographic Atrophy Secondary to Age-Related Macular Degeneration

DateMay 2, 2022

Conference/JournalARVO Annual Meeting 2022

Jared S Nielsen, MD, MBA read more

CFI Supplementing Gene Therapy in Geographic Atrophy: FOCUS Phase I/IIa Clinical Trial Update

DateFeb 11, 2022

Conference/JournalAngiogenesis, Exudation, and Degeneration 2022

Waheed N K read more

Delivering Investigational Gene Therapy, GT005, via the Orbit™ Subretinal Delivery System in the Phase I/II FOCUS Clinical Trial. Excerpted from Presentation: “Delivery Strategies for Gene and Cell Therapies in Retinal Disease”

DateNov 13, 2021

Conference/JournalAmerican Academy of Ophthalmology (AAO): Retina Subspecialty Day

Allen Ho, MD read more

Interim Results from a First-in-Human Phase I/II Gene Therapy Study (FOCUS) of GT005, an Investigational AAV2 Vector Encoding Complement Factor I (CFI), in Patients with Geographic Atrophy (GA)

DateSep 30, 2021

Conference/JournalRetina Society

Szilárd Kiss, MD read more

Preliminary results from a first-in-human Phase I/II gene therapy study (FOCUS) of GT005, an investigational AAV2 vector encoding complement factor I, in patients with geographic atrophy

DateSep 10, 2021

Conference/JournalEURETINA 2021

MacLaren R E read more

Functional Expression of Complement Factor I Following AAV-mediated gene delivery in the Retina of Mice and Human Cells

DateMar 10, 2021

Conference/JournalGene Therapy

Dreismann A K et al read more

FOCUS Interim Results: GT005 Gene Therapy Phase I/II Study for the Treatment of Geographic Atrophy

DateFeb 12, 2021

Conference/JournalAngiogenesis, Exudation, and Degeneration 2021

Waheed N K read more

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